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TREAT-NMD stakeholder meeting for natural history studies in limb girdle muscular dystrophy 18th June 2019, Amsterdam, The Netherlands

  • Author Footnotes
    1 These authors contributed equally to this work.
    Michela Guglieri
    Footnotes
    1 These authors contributed equally to this work.
    Affiliations
    The John Walton Muscular Dystrophy Research Center, Newcastle University and Newcastle Hospitals NHS Foundation Trust, The International Centre for Life, Central Parkway, Newcastle upon Tyne NE1 3BZ, UK
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  • Author Footnotes
    1 These authors contributed equally to this work.
    Jordi Díaz-Manera
    Footnotes
    1 These authors contributed equally to this work.
    Affiliations
    The John Walton Muscular Dystrophy Research Center, Newcastle University and Newcastle Hospitals NHS Foundation Trust, The International Centre for Life, Central Parkway, Newcastle upon Tyne NE1 3BZ, UK

    Neuromuscular Disorders Unit, Neurology Department, Hospital de la Santa Creu I Sant Pau, de Barcelona, Spain
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  • Volker Straub
    Correspondence
    Corresponding author.
    Affiliations
    The John Walton Muscular Dystrophy Research Center, Newcastle University and Newcastle Hospitals NHS Foundation Trust, The International Centre for Life, Central Parkway, Newcastle upon Tyne NE1 3BZ, UK
    Search for articles by this author
  • Author Footnotes
    1 These authors contributed equally to this work.

      Highlights

      • Overview of current and planned natural history studies for the limb girdle muscular dystrophies.
      • Overview of outcome measures being employed for the limb girdle muscular dystrophies.
      • Identification of actions to inform care guidelines for the limb girdle muscular dystrophies.

      Keywords

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