Highlights
- •Overview of the multiple dystrophin isoforms expressed in the brain.
- •Large body of preclinical data and possibilities for postnatal dystrophin restoration.
- •Overview of neurocognitive and behavioral heterogeneity in DMD and BMD.
- •Neuromuscular specialists to also focus on early diagnosis and intervention for brain comorbidities.
- •Need to develop standard operation procedures for neurocognition and behavior assessment.
Keywords
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Article info
Publication history
Published online: August 14, 2020
Received in revised form:
July 27,
2020
Received:
July 14,
2020
