Neuromuscular Disorders
Volume 19, Issue 8 , Page 602, September 2009

M.P.3.04 Assessment of StepWatch™ activity monitoring in phase 2b study of ataluren (PTC124™) in nmDMD/BMD

  • C. McDonald

      Affiliations

    • University of California, Davis School of Medicine, Davis, CA, United States
  • ,
  • K. Coleman

      Affiliations

    • Orthocare Innovations, Seattle, WA, United States
  • ,
  • E. Henricson

      Affiliations

    • University of California, Davis School of Medicine, Davis, CA, United States
  • ,
  • R.T. Abresch

      Affiliations

    • University of California, Davis School of Medicine, Davis, CA, United States
  • ,
  • M. Eagle

      Affiliations

    • Institute of Human Genetics, Newcastle University, Newcastle upon Tyne, United Kingdom
  • ,
  • J. Florence

      Affiliations

    • Washington University School of Medicine, St. Louis, MO, United States
  • ,
  • E. Gappmaier

      Affiliations

    • University of Utah, Salt Lake City, UT, United States
  • ,
  • A.M. Glanzman

      Affiliations

    • Children’s Hospital of Philadelphia, Philadelphia, PA, United States
  • ,
  • A. Reha

      Affiliations

    • PTC Therapeutics, Inc., South Plainfield, NJ, United States
  • ,
  • G.L. Elfring

      Affiliations

    • PTC Therapeutics, Inc., South Plainfield, NJ, United States
  • ,
  • L.L. Miller

      Affiliations

    • PTC Therapeutics, Inc., South Plainfield, NJ, United States
  • ,
  • L. Atkinson

      Affiliations

    • PTC Therapeutics, Inc., South Plainfield, NJ, United States

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PII: S0960-8966(09)00342-3

doi:10.1016/j.nmd.2009.06.185

Neuromuscular Disorders
Volume 19, Issue 8 , Page 602, September 2009