Neuromuscular Disorders
Volume 18, Issue 11 , Pages 894-903 , November 2008

Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; Report of three expert workshops: TREAT-NMD/ENMC Workshop on outcome measures, 12th–13th May 2007, Naarden, The Netherlands; TREAT-NMD Workshop on outcome measures in experimental trials for DMD, 30th June–1st July 2007, Naarden, The Netherlands; Conjoint Institute of Myology TREAT-NMD Meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

  • E. Mercuri

      Affiliations

    • Department of Paediatric Neurology, Catholic University, Rome, Italy
    • Corresponding Author InformationCorresponding author. Address: Department of Child Neurology, Policlinico Gemelli, Largo Gemelli 00168, Roma, Italy. Tel.: +39 06 30155340; fax: +39 06 30154363.
    • ,
  • A. Mayhew

      Affiliations

    • Dubowitz Neuromuscular Unit, Institute of Child Health, University College London, UK
    • ,
  • F. Muntoni

      Affiliations

    • Dubowitz Neuromuscular Unit, Institute of Child Health, University College London, UK
    • ,
  • S. Messina

      Affiliations

    • Department of Paediatric Neurology, Catholic University, Rome, Italy
    • ,
  • V. Straub

      Affiliations

    • Institute of Human Genetics, University of Newcastle upon Tyne, International Centre for Life, Newcastle upon Tyne, UK
    • ,
  • G.J. Van Ommen

      Affiliations

    • Center for Human and Clinical Genetics, Leiden University Medical Center, Leiden, The Netherlands
    • ,
  • T. Voit

      Affiliations

    • Institut de Myologie Université Pierre et Marie Curie Paris VI, Groupe Hospitalier Pitié-Salpêtrière, Paris, France
    • ,
  • E. Bertini

      Affiliations

    • Department of Laboratory Medicine, Unit of Molecular Medicine, Bambino Gesù Hospital, Rome, Italy
    • ,
  • K. Bushby

      Affiliations

    • Institute of Human Genetics, University of Newcastle upon Tyne, International Centre for Life, Newcastle upon Tyne, UK
    • ,
  • On behalf of the TREAT-NMD Neuromuscular Network

,Revised 17 June 2008 ,Accepted 11 July 2008.

References 

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PII: S0960-8966(08)00571-3

doi: 10.1016/j.nmd.2008.07.003

Neuromuscular Disorders
Volume 18, Issue 11 , Pages 894-903 , November 2008

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