Neuromuscular Disorders
Volume 18, Issue 9 , Pages 832-833, October 2008

T.O.4 Safety and efficacy results from a randomized, double-blind, placebo-controlled study of alglucosidase alfa for the treatment of Pompe disease in juveniles and adults

  • P. Laforet

      Affiliations

    • Institut de Myologie, Groupe Hospitalier Pitie-Salpetriere, Paris, France
    • ,
  • P.R. Clemens

      Affiliations

    • University of Pittsburgh, Department of Neurology, Pittsburgh, United States
    • ,
  • D. Corzo

      Affiliations

    • Genzyme Corporation, Cambridge, United States
    • ,
  • D. Escolar

      Affiliations

    • Children’s National Medical Center, Washington, DC, United States
    • ,
  • J. Florence

      Affiliations

    • Washington University, School of Medicine, St. Louis, United States
    • ,
  • A. van der Ploeg

      Affiliations

    • Erasmus Medical Center, Rotterdam, The Netherlands
    • ,
  • S. Lake

      Affiliations

    • Genzyme Corporation, Cambridge, United States
    • ,
  • J. Mayhew

      Affiliations

    • Children’s National Medical Center, Washington, DC, United States
    • ,
  • A. Pestronk

      Affiliations

    • Washington University, School of Medicine, St. Louis, United States
    • ,
  • B. Rosenbloom

      Affiliations

    • Tower Hematology Oncology, Beverly Hills, United States
    • ,
  • A. Skrinar

      Affiliations

    • Genzyme Corporation, Cambridge, United States
    • ,
  • M. Wasserstein

      Affiliations

    • Mount Sinai School of Medicine, New York, United States

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PII: S0960-8966(08)00545-2

doi:10.1016/j.nmd.2008.06.379

Neuromuscular Disorders
Volume 18, Issue 9 , Pages 832-833, October 2008

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