G.P.1 01 Clinical presentation and disease progression in late-onset Pompe disease

1 Children’s National Medical Center, Washington, DC, USA

2 University Medical Center Utrecht, Utrecht, The Netherlands

3 Washington University in St. Louis, St. Louis, MO, USA

4 Children’s Hospital and Medical Center, Seattle, WA, USA

5 Institut de Myologie, Groupe Hospitalier Pitié-Salpêtrière, Paris, France